Gene therapy restores immune function and extends lives of children with rare immune disorder Gene Therapy Journal
Therapeutic ex vivo gene transfer into autologous hematopoietic stem cells, referred to here as gene therapy, may provide a long-term and Muscle-Targeted Gene Therapy Using Engineered Viruses | New Breakthrough from Cell Journal Journal Club | Developing a Novel Gene Therapy for Kcnv2 Retinopathy The Journal of Gene Medicine is an international gene therapy journal publishing advances in genetic medicine of relevance to genomics, oncology, neuroscience, ...